The SCN8A Global Research Roadmap is a groundbreaking initiative that's transforming the future for individuals living with SCN8A-related disorders. We’ve united families, researchers, clinicians, and pharmaceutical companies to address the most pressing challenges in SCN8A research and care.
Key Priorities:
- Developing genetic therapies that could change the course of SCN8A.
- Improving non-seizure outcomes like communication, behavior, and motor function.
- Optimizing current treatments to provide better care today.
- Advancing biomarker research to track disease progression and treatment effectiveness.
- Collaborating across rare diseases to accelerate breakthroughs.
Your donation will directly fund research that can bring life-changing therapies to those affected by SCN8A. Join us in making the future brighter for children and families living with SCN8A.
Together, we can drive research forward and deliver real hope.
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